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FDA SEEKS LARGER TRIAL OF PROMISING DRUG TO TREAT MUSCULAR DYSTROPHY

 

By Miriam Raftery

April 21, 2014 (Washington D.C.) --The U.S. Food and Drug Administration, or FDA, is on the verge of approving the first-ever drug treatment for a severe form of muscular dystrophy.  Duchenne muscular dystrophy is a deadly disease that typically  leaves its victims in wheelchairs by their teens and dead in their 20s, according to the U.S. Human Genome Institute.  This disease strikes one in every 3500 boys worldwide.


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